Retinal Diseases Caused by RPE65 Mutations clinical trials at UC Davis

1 research study open to eligible people

HG004 for Leber Congenital Amaurosis Related to Rpe65 Gene Mutations (STAR)
“Volunteer for research and contribute to discoveries to help us better understand Leber Congenital Amaurosis!”
open to eligible people ages 6-50
The purpose of the study is to determine whether HG004 as gene therapy is safe and effective for the treatment of Leber Congenital Amaurosis caused by mutations in RPE65 gene.
Sacramento, California and other locations

Last updated: September 2024